Viral gene editing system corrects genetic liver disease in newborn mice
Monday, February 1, 2016 - 13:46
in Health & Medicine
For the first time, researchers have treated an animal model of a genetic disorder using a viral vector to deliver genome-editing components in which the disease- causing mutation has been corrected. Delivery of the vector to newborn mice improved their survival while treatment of adult animals, unexpectedly, made them worse.