FDA: Duchenne muscular dystrophy drug not ready for approval
Thursday, January 14, 2016 - 12:39
in Health & Medicine
Stephen FellerSILVER SPRING, Md., Jan. 14 (UPI) -- FDA denies approval for BioMarin Pharmaceutical's drisapersen, a drug to treat Duchenne muscular dystrophy, saying it has not met requirements for efficacy.