Giant axonal neuropathy: Researchers develop innovative gene transfer-based treatment approach
Thursday, June 25, 2015 - 20:00
in Health & Medicine
Researchers have developed an innovative, experimental gene transfer-based treatment for children with giant axonal neuropathy (GAN). This extremely rare genetic disorder causes children to gradually lose the ability to balance themselves, move their muscles and to feel certain sensations. Most children born with GAN do not survive beyond their early 20s because of progressive impairment of their ability to breath.