Gene therapy breakthrough heralds treatment for beta-thalassemia

Italian scientists pioneering a new gene transfer treatment for the blood disorder beta-thalassemia have successfully completed preclinical trials, claiming they can correct the lack of beta-globin in patients' blood cells which causes the disease. The research, published in EMBO Molecular Medicine, reveals how gene therapy may represent a safe alternative to current cures that are limited to a minority of patients...

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