Testing the efficacy of new gene therapies more efficiently
Tuesday, March 21, 2017 - 13:03
in Health & Medicine
Using a new cellular model, innovative gene therapy approaches for the hereditary immunodeficiency Chronic Granulomatous Disease can be tested faster and cost-effectively in the lab for their efficacy. A team of researchers has successfully achieved this using the 'gene-scissor' CRISPR/Cas9 technology. The aim is to treat severely affected patients in the near future using novel approaches.