Mechanistic insights into spinal muscular atrophy suggest new paths for treatment
Tuesday, January 13, 2015 - 00:01
in Health & Medicine
New light has been shed on the underlying pathology of spinal muscular atrophy, a rare but devastating disease that causes muscle weakness and paralysis and is the leading genetic cause of infant deaths. With no approved drugs currently available, the newly obtained insights may prove valuable as scientists currently work to define optimal treatment strategies for patients.