Promising First-in-class Drug Candidate For Genetic Protein-misfolding Disease
Thursday, July 23, 2009 - 00:28
in Health & Medicine
A promising new drug candidate -- the first in its class -- has been discovered for patients with a genetic protein-misfolding disease. The new drug tafamidis significantly halts disease progression for patients with a disease called Transthyretin (TTR) amyloid polyneuropathy (ATTR-PN).