Scientists uncover most detailed picture yet of muscular dystrophy defect then design targeted new drug candidates
Thursday, January 2, 2014 - 14:00
in Biology & Nature
Scientists have revealed an atomic-level view of a genetic defect that causes a form of muscular dystrophy, myotonic dystrophy type 2, and have used this information to design drug candidates with potential to counter those defects—and reverse the disease.